- Khondrion presents Phase II KHENERGY Trial Data
- UMDF joins NORD statement Statement in Opposition to the Senate’s Proposed Weakening of the Orphan Drug Tax Credit
- Stealth BioTherapeutics Initiates Phase 3 Study of Elamipretide in Patients with Primary Mitochondrial Myopathy
- New clinical care guidelines issued for patients with mitochondrial disease.
- KH176 under development for rare mitochondrial disease: a first in man randomized controlled clinical trial in healthy male volunteers.