FOR IMMEDIATE RELEASE June 25, 2018 Contact: Clifford F. Gorski UMDF Director of Communications 412.793.8077 – firstname.lastname@example.org (Pittsburgh, PA) The United Mitochondrial Disease Foundation (UMDF) announced that its board of trustees chose Brian Harman as the organization’s next chief executive officer and president. Harman will begin his new role with UMDF on July [...]
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So far Cliff Gorski has created 82 blog entries.
CHOP Researchers: Patient-Centric Perspective Offers Key Insights into Upcoming Treatment Studies Philadelphia, June 6, 2018 – As clinical trials gear up with the aim of attaining the first FDA-approved treatments for mitochondrial disease, a new study reports for the first time what patients and families say would motivate them for or against participating in [...]
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Stealth BioTherapeutics Granted Orphan Drug Designation of Elamipretide for Treatment of Leber’s Hereditary Optic NeuropathyCliff Gorski2018-04-30T10:06:05+00:00
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Click here to see the information on this paper. Listen to the Podcast with Dr. Hirano and Dr. Thompson
GenSight has demonstrated that its gene therapy for a rare disease causing blindness can significantly improve the vision of LHON patients.Cliff Gorski2018-04-04T13:09:37+00:00
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Preclinical Testing in 3 Model Systems Suggests Some Antioxidants May Be Effective Mitochondrial Disease TreatmentsCliff Gorski2018-03-27T12:48:54+00:00
Preclinical Testing in 3 Model Systems Suggests Some Antioxidants May Be Effective Mitochondrial Disease Treatments --CHOP Researchers Test 7 Compounds in Seeking Candidates for Clinical Trials; Early Efficacy Seen in NAC and Vitamin E-- Philadelphia, March 27, 2018 – A systematic study of seven antioxidants commonly taken by or suggested to benefit children [...]
See the letter by patient advovcacy groups in opposition here.