The Critical Role of Patients in Rare Disease Clinical Trials

The Critical Role of Patients in Rare Disease Clinical Trials January 28, 2019 12pm EST (9am PST) Presented by Cristy Balcells RN MSN & James Valentine JD MHS This is a free informational webinar, forum and opportunity to ask questions, offered in partnership by MitoAction, UMDF and Stealth BioTherapeutics. Learn how to search, find, and […]

Clinical Trial For Patients with PDCD

Clinical Trial For Patients With Genetically Confirmed Pyruvate Dehydrogenase Complex (PDC) Registration for this new clinical trial, Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency: (DCA/PDCD), is now open for patients who are ages 6 months through 17. This is a study of an investigational drug called sodium dichloroacetate (DCA). Investigational means that the study […]