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So far Cliff Gorski has created 60 blog entries.
Stealth BioTherapeutics Granted Orphan Drug Designation of Elamipretide for Treatment of Leber’s Hereditary Optic NeuropathyCliff Gorski 2018-04-30T10:06:05+00:00
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Click here to see the information on this paper. Listen to the Podcast with Dr. Hirano and Dr. Thompson
GenSight has demonstrated that its gene therapy for a rare disease causing blindness can significantly improve the vision of LHON patients.Cliff Gorski 2018-04-04T13:09:37+00:00
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Preclinical Testing in 3 Model Systems Suggests Some Antioxidants May Be Effective Mitochondrial Disease TreatmentsCliff Gorski 2018-03-27T12:48:54+00:00
Preclinical Testing in 3 Model Systems Suggests Some Antioxidants May Be Effective Mitochondrial Disease Treatments --CHOP Researchers Test 7 Compounds in Seeking Candidates for Clinical Trials; Early Efficacy Seen in NAC and Vitamin E-- Philadelphia, March 27, 2018 – A systematic study of seven antioxidants commonly taken by or suggested to benefit children [...]
See the letter by patient advovcacy groups in opposition here.
Intravenous Arginine Benefits Children after Acute Metabolic Strokes — CHOP Researchers Find Notable Responses, No Adverse Events in Children with Mitochondrial DiseaseCliff Gorski 2018-03-09T11:09:56+00:00
FOR IMMEDIATE RELEASE Friday, March 9, 2018 John Ascenzi Children’s Hospital of Philadelphia (267) 426-6055 Ascenzi@email.chop.edu Intravenous Arginine Benefits Children after Acute Metabolic Strokes --CHOP Researchers Find Notable Responses, No Adverse Events in Children with Mitochondrial Disease-- Philadelphia, March 9, 2018 – Children with mitochondrial diseases who suffered acute metabolic strokes benefited from [...]
Reata Announces Top-Line Data from the Dose-Escalation Cohorts of the Phase 2 Motor Study of Omaveloxolone in Patients With Mitochondrial Myopathies.Cliff Gorski 2018-03-05T09:11:37+00:00
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